Have you ever wished you could tell the people who research, develop, and regulate treatments for CTX what’s most important to you? You can! At the “Unlock CTX” Patient-Focused Drug Development Meeting.
For the first time, people living with CTX and those who care for and about them are invited to share their experiences with the people who research, develop, and regulate treatments for CTX.
On September 14, 2021 from 11:00 AM – 3:00 PM Eastern time, the first patient-focused drug development (PFDD) meeting dedicated to CTX will be held VIRTUALLY. Participants from across the globe are invited to take part.
The United Leukodystrophy Foundation and the CTX community have joined together to make sure FDA staff, drug and medical device developers, and other stakeholders hear directly from people living with CTX about the many burdens of the condition and the treatment outcomes that matter most to them.
Thank you to our partner organizations for their support and promotion of the Unlock CTX PFDD Initiative:
Thank you to these generous sponsors for their unrestricted educational grants in support of the Unlock CTX PFDD initiative: